betibeglogene autotemcel (beti-cel) One-Time Gene Therapy for β-thalassemia Continues to Demonstrate Durable Efficacy Across Pediatric and Adult Patient Populations and All Genotypes in Data Presented ...
(RTTNews) - An advisory committee to the U.S. Food and Drug Administration voted unanimously to recommend approval of bluebird bio Inc.'s (BLUE) beti-cel gene therapy for people with beta-thalassemia ...